MIDDLETON, Mass., Nov. 6, 2025 /PRNewswire/ -- MavriX Bio, a clinical-stage biotechnology company focused on the development of transformative genetic therapies for Angelman syndrome (AS), today ...
Take advantage of TipRanks Premium at 50% off! Unlock powerful investing tools, advanced data, and expert analyst insights to help you invest with confidence. Ultragenyx Pharmaceutical ( (RARE)) just ...
Angelman syndrome (AS) is a rare neurodevelopmental disorder caused by the loss of function of the maternally inherited ubiquitin E3 ligase UBE3A gene. AS is characterized by severe symptoms, ...
Carla Peoples says she'd been “totally healthy” all her life when she noticed subtle changes in her body. There was some bloating that progressed to the point where it caused her belly stick out. “I ...
On Tuesday, the U.S. Food and Drug Administration (FDA) granted Breakthrough Therapy designation to Ionis Pharmaceuticals Inc.’s (NASDAQ:IONS) ION582 for Angelman syndrome (AS), a rare neurological ...
CARLSBAD, Calif.--(BUSINESS WIRE)--Ionis Pharmaceuticals, Inc. (Nasdaq: IONS) today announced that the U.S. Food and Drug Administration (FDA) has granted Breakthrough Therapy designation to ION582 ...
In the run-up to menopause, known as perimenopause, women typically are beset with hot flashes, night sweats, vaginal dryness, and sleep and mood disturbances, triggered by a decline in estrogen ...
Broken Hill man Mitch McKenny plans to run from the outback city to Newcastle in 29 days. He aims to raise awareness and funds for Angelman syndrome, a rare genetic disorder. Tradie 'fed up' as ...
For a decade, Holli Barron went in and out of doctor's offices, desperate for answers to a growing list of mysterious symptoms—throat swelling, rashes, extreme fatigue, and more. Despite receiving ...
A woman who spent over a decade struggling with painful symptoms and had to wait helplessly as her health declined has finally discovered the cause—she never would have predicted it. Laura Schaeffer ...
After many years and multiple doctors visits, a New York woman finally has answers to a medical mystery that drastically altered her life. Maureen Henry, of Rockland County, said she experienced ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback