Cure SMA Welcomes Broad FDA Approval of Itvisma(TM) for Spinal Muscular Atrophy, Reinforces Commitment to Patient Access and Support

SCHAUMBURG, Ill., Nov. 26, 2025 /PRNewswire/ -- Cure SMA, the leading nonprofit organization dedicated to supporting those impacted by spinal muscular atrophy (SMA), welcomes the FDA approval of ...
Healio

FDA approves Itvisma in spinal muscular atrophy for patients aged 2 years and older

The FDA has approved an adeno-associated virus 9 gene replacement therapy to treat individuals aged 2 years and older with ...
pharmaphorum

Manufacturing issues block FDA nod for Scholar Rock SMA drug

Unresolved compliance issues at a manufacturing plant operated by Novo Nordisk have led to a complete response letter for Scholar Rock's lead drug for spinal muscular atrophy (SMA). The CRL is related ...
Healthline

What's the Difference Between Ischemic Colitis and Mesenteric Ischemia?

Ischemic colitis and mesenteric ischemia are both types of bowel ischemia. Ischemic colitis refers to reduced blood flow to the large intestine, while mesenteric ischemia happens due to reduced blood ...
WebMD

What Is Mast Cell Activation Syndrome?

Mast cell activation syndrome is a condition that causes mast cells to release an inappropriate amount of chemicals into your body. This causes allergy symptoms and a wide range of other symptoms.
The Citizen

Watch: Teen with rare syndrome melts hearts with reaction to Springbok card

As a tiny tot, he would stand with his hand on his chest, eyes closed, and sing every word of the national anthem – long before the Springboks were the world champions they are today. Now, at the age ...
iaea.org

Radiation protection of pregnant women in radiology

» Is there a safe level of radiation exposure for a patient during pregnancy? Dose limits do not apply for radiation exposure of patients, since the decision to use radiation is justified depending ...
Healthline

Birth Order and Personality: The Science Behind Middle Child Syndrome

If you are a middle child, or have a sibling who is a middle child, you may be wondering if “middle child syndrome” is a real thing. Middle child syndrome is the belief that middle children are ...
Investopedia

Separate Accounts Explained: How They Work and Key Benefits

James Chen, CMT is an expert trader, investment adviser, and global market strategist. Thomas J. Brock is a CFA and CPA with more than 20 years of experience in various areas including investing, ...
SMA

First-line gene therapy may offer better sustained results in SMA

First-line Zolgensma (onasemnogene abeparvovec-xioi) outperformed first-line Spinraza (nusinersen) in achieving a more sustained clinical response and reducing the need for supportive care among young ...
casereports.bmj

Superior mesenteric artery syndrome as a cause of acute pancreatitis

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