Encoded Therapeutics Inc., a clinical-stage biotechnology company developing genetic medicines for severe neurological disorders, today announced positive interim results from its ongoing POLARIS ...
3d
Ionis receives U.S. FDA Breakthrough Therapy designation for zilganersen for Alexander disease (AxD)
Ionis Pharmaceuticals, Inc. (Nasdaq: IONS) today announced that the U.S. Food and Drug Administration (FDA) has granted ...
SCOTTSDALE, Ariz. (InvestigateTV) — Patients are coming from around the world to Scottsdale to see the only neurosurgeon in the state performing a groundbreaking surgery that provides life-changing ...
MIDDLETON, Mass., Nov. 6, 2025 /PRNewswire/ -- MavriX Bio, a clinical-stage biotechnology company focused on the development of transformative genetic therapies for Angelman syndrome (AS), today ...
Liliana Castaneda, with Turner syndrome, was diagnosed with rare clear cell carcinoma of the vagina at 14, unrelated to her condition. Her treatment involved five chemotherapy rounds, external beam ...
CAROLINA FOREST, SC (WMBF) - A Carolina Forest teenager is sharing her terrifying brush with death to warn other families about a rare but potentially deadly condition. Sixteen-year-old Brynn Dietrich ...
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