Oliver Chu is one of five kids participating in a clinical trial investigating a gene therapy for Hunter syndrome, a disorder with symptoms akin to childhood dementia that limits life expectancy ...
Dr. J. Westley Ohman discusses screening protocols, how connective tissue disorders inform decision-making, advice for ...
A $100,000 grant awarded to researchers at UTHealth Houston from the John Ritter Foundation will fund an app that will help ...
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Toddler with Down Syndrome loves his reflection
What a gorgeous reflection 🥰 He couldn't stop smiling 🥰 Trump panics over a White House mirror during meeting Mystery object hits United flight at 36,000 feet; Passenger describes terrifying moments ...
ROANOKE, Va. (WDBJ) - For the past seven years, Gunnar Boothe has made the hockey rink his home. As a member of the Roanoke Junior Rail Yard Dawgs, Gunnar had a standout performance as goalie in 2024, ...
Selected from thousands worldwide, a Tenn. toddler with rare Down syndrome will make a Times Square jumbotron debut. Trump admin hands immigrant farm workers major win There Are Mystery Rings Around ...
Legend Whaley, one of only 250 recorded cases worldwide of rare Down syndrome form, selected from global entries for National Down Syndrome Society Buddy Walk Times Square jumbotron appearance MT.
Dancing around the house to Taylor Swift’s "Welcome to New York," Emery Tanner, a 4-year-old from Lafayette, is gearing up to represent the Down syndrome community in New York’s Times Square.
One of the priority objectives of research into rare diseases is to develop new treatments, and orphan medicines — which target conditions affecting no more than 5 in 10,000 people in the EU — provide ...
The European Medicines Agency (EMA) has designated allopurinol as the first orphan drug for the treatment of Marfan syndrome, a rare connective tissue disease which as no cure to date. This disease ...
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