Ionis receives U.S. FDA Breakthrough Therapy designation for zilganersen for Alexander disease (AxD)

Ionis Pharmaceuticals, Inc. (Nasdaq: IONS) today announced that the U.S. Food and Drug Administration (FDA) has granted ...
Morningstar

MavriX Bio Announces First Patient Dosed in ASCEND-AS Trial of MVX-220, Investigational Gene Therapy for Angelman Syndrome

MIDDLETON, Mass., Nov. 6, 2025 /PRNewswire/ -- MavriX Bio, a clinical-stage biotechnology company focused on the development of transformative genetic therapies for Angelman syndrome (AS), today ...
WDSU

Buddy Walk to highlight the 'can do' spirit of local people with Down syndrome

DRAGO’S IN METAIRIE. THERE IS STILL TIME TO SIGN UP FOR THIS WEEKEND’S BUDDY WALK, AND SHOW YOUR SUPPORT FOR PEOPLE WITH DOWN SYNDROME IN THE NEW ORLEANS AREA. THE DOWN SYNDROME ASSOCIATION OF GREATER ...
Hosted on MSN

Ultragenyx Begins Dosing in Aurora Study for Angelman Syndrome

Take advantage of TipRanks Premium at 50% off! Unlock powerful investing tools, advanced data, and expert analyst insights to help you invest with confidence. Ultragenyx Pharmaceutical ( (RARE)) just ...
The Bulletin

Successful Step Up Walk for Down Syndrome held at Fontaine Field in Norwich

More than 130 people gathered at Fontaine Field in Norwich Oct. 11 for a community walk supporting individuals with Down Syndrome. The event marked the first annual Step Up Walk for Down Syndrome in ...
news10nbc

People with Down syndrome and their families connect at annual Buddy Walk

RUSH, N.Y. — The Flower City Down Syndrome Network hosted its 29th annual Buddy Walk on Sunday at the Rochester Rotary Sunshine Camp in Rush. The walk brings together hundreds of people for a scenic ...
10 News

Dozens of families gathered at World's Fair Park for Knoxville Buddy Walk

KNOXVILLE, Tenn. — Sunday afternoon, dozens of East Tennessee families gathered in the World's Fair Park for the Knoxville Buddy Walk, hosted by the Down Syndrome Awareness Group of East Tennessee.
Post and Courier

Aiken Buddy Walk celebrates people with Down Syndrome, advocates inclusion

Inclusion and celebration of people with Down Syndrome was theme of the day Oct. 19 at the 2025 Aiken Buddy Walk, an annual event held by Upside of Downs of Aiken. Held on the campus of USC Aiken, the ...
WTOC-TV

Lowcountry Down Syndrome Society celebrates 20th annual Buddy Walk in Forsyth Park

SAVANNAH, Ga. (WTOC) - Over 3,000 people headed to Forsyth Park Saturday for the 20th Annual Buddy Walk, hosted by the Lowcountry Down Syndrome Society. The event kicked off Saturday morning at 10:00 ...
WOWT.com

Omaha man to walk in Global Down Syndrome Foundation’s Fashion Show

OMAHA, Neb. (WOWT) - It’s through listening and studying music that James or “boby” can just be himself. It can also help when dealing with the loss of his parents. Though he can’t always verbalize it ...
WFLA News Channel 8

Buddy Walk raises funds, awareness for individuals with Down syndrome in Tampa

HILLSBOROUGH COUNTY, Fla. (WFLA) – The Buddy Walk in Tampa is breaking its own record for fundraising and number of participants. The 9th annual event raises awareness about Down syndrome. With the ...